Philip Kranz researcher, Natalie McGauran researcher, Rita Banzi researcher, Can Ünal researcher, Fabian Lotz researcher, Thomas Kaiser director et al
Kranz P, McGauran N, Banzi R, Ãœnal C, Lotz F, Kaiser T et al.
Reforming EU and national orphan drug regulations to improve outcomes for patients with rare diseases
BMJ 2023; 381 :e072796
doi:10.1136/bmj-2022-072796
