Feature Drug Regulation What makes an orphan drug? BMJ 2010; 341 doi: https://doi.org/10.1136/bmj.c6459 (Published 17 November 2010) Cite this as: BMJ 2010;341:c6459 Article Related content Metrics Responses Peer review Related articles Observations Open letter to prime minister David Cameron and health secretary Andrew Lansley Published: 17 November 2010; BMJ 341 doi:10.1136/bmj.c6466 Analysis Orphan drug pricing may warrant a competition law investigation Published: 17 November 2010; BMJ 341 doi:10.1136/bmj.c6471 Letter Regulation is flawed Published: 07 December 2010; BMJ 341 doi:10.1136/bmj.c7016 Editorial The problem of orphan drugs Published: 17 November 2010; BMJ 341 doi:10.1136/bmj.c6456 Editor's Choice Stop exploiting orphan drugs Published: 18 November 2010; BMJ 341 doi:10.1136/bmj.c6587 See more Maternal deaths from suicide must be tackled, say experts BMJ December 07, 2016, 355 i6585; DOI: https://doi.org/10.1136/bmj.i6585 Andrew Wakefield calls Trump “on our side” over vaccines after meeting BMJ December 05, 2016, 355 i6545; DOI: https://doi.org/10.1136/bmj.i6545 The future of NHS dentistry in Scotland BMJ December 05, 2016, 355 i6466; DOI: https://doi.org/10.1136/bmj.i6466 South Africa begins first HIV vaccine trial in seven years BMJ December 01, 2016, 355 i6501; DOI: https://doi.org/10.1136/bmj.i6501 Better evidence for smarter policy making BMJ December 01, 2016, 355 i6399; DOI: https://doi.org/10.1136/bmj.i6399 Cited by... Application of orphan drug designation to cancer treatments (2008-2017): a comprehensive and comparative analysis of the USA and EU