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Child in gene therapy programme develops leukaemia

BMJ 2008; 336 doi: https://doi.org/10.1136/bmj.39436.582292.DB (Published 03 January 2008) Cite this as: BMJ 2008;336:13
  1. Andrew Cole
  1. 1London

    Doctors at Great Ormond Street Hospital for Children in London have admitted that other children may be at risk after leukaemia was diagnosed in a child on its pioneering gene therapy programme.

    The unnamed 3 year old was taking part in a clinical trial treating children for X linked severe combined immunodeficiency (X-SCID), also known as “baby in the bubble syndrome,” in which boys are born with no immune system. Around six to eight children are affected by the condition each year in the United Kingdom.

    The trial, which began at Great Ormond Street in 2001 and ended earlier this year, involved 10 children …

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