Gene therapy saves immune deficient babies in FranceBMJ 2000; 320 doi: https://doi.org/10.1136/bmj.320.7244.1225 (Published 06 May 2000) Cite this as: BMJ 2000;320:1225
- Roger Dobson
Gene therapy has been successfully used by French researchers to treat severe combined immunodeficiency (SCID). Two babies, aged 8 and 11 months, who received the treatment are no longer in isolation and live at home without any treatment, enjoying normal growth and development for their ages.
The normal functioning of the infants' immune system has lasted 11 months without any side effects so far, and a third patient is making similar progress four months after …